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Real-world Impact of Gene Therapy: A Patient Story from New Jersey

We share a report about a 21-year-old student and his journey living with a rare disease.

Story
Explore real-life experiences in managing hemophilia with an illustration of a blood droplet

Gene therapy is now available for the treatment of hemophilia B in multiple countries, making appropriate adults eligible for this innovative treatment. CSL is proud to share stories of individuals who have received gene therapy, showcasing the real-world impact of this medical advancement.

Read a patient story from BlackDoctor.org

Read a patient story from PhillyVoice

Read a patient story from Hemophilia News Today